Cut and Paste: Treating Spinal Muscular Atrophy with Nusinersen

Cut and Paste: Treating Spinal Muscular Atrophy with Nusinersen

How Spinraza (nusinersen) and Evrysdi treat Spinal Muscular Atrophy (SMA) through splice-switchingПодробнее

How Spinraza (nusinersen) and Evrysdi treat Spinal Muscular Atrophy (SMA) through splice-switching

Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?Подробнее

Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?

Spinal Muscular Atrophy 2019: Approved Treatment and Upcoming Therapeutic StrategiesПодробнее

Spinal Muscular Atrophy 2019: Approved Treatment and Upcoming Therapeutic Strategies

Colorado Virtual Education Screening: Spinal Muscular Atrophy (SMA)Подробнее

Colorado Virtual Education Screening: Spinal Muscular Atrophy (SMA)

Nusinersen (SpinrazaTM): The First FDA Approved Treatment for SMAПодробнее

Nusinersen (SpinrazaTM): The First FDA Approved Treatment for SMA

SPINRAZA® (nusinersen) Mechanism of Action in Spinal Muscular AtrophyПодробнее

SPINRAZA® (nusinersen) Mechanism of Action in Spinal Muscular Atrophy

Nusinersen: ASO(Anti-Sense- Oligonucleotide) Therapy toward Spinal Muscular Atrophy (SMA) #Code: 198Подробнее

Nusinersen: ASO(Anti-Sense- Oligonucleotide) Therapy toward Spinal Muscular Atrophy (SMA) #Code: 198

New Clinical Data on Adult Nusinersen treated Patients with SMAПодробнее

New Clinical Data on Adult Nusinersen treated Patients with SMA

Nusinersen Treatment for Older Patients with SMAПодробнее

Nusinersen Treatment for Older Patients with SMA

Nusinersen: The First Approval for Spinal Muscular AtrophyПодробнее

Nusinersen: The First Approval for Spinal Muscular Atrophy

Treating spinal muscular atrophy in adult patientsПодробнее

Treating spinal muscular atrophy in adult patients

Nusinersen Treatment Outcomes in Later Onset SMAПодробнее

Nusinersen Treatment Outcomes in Later Onset SMA

Real-World Experience Treating SMA With NusinersenПодробнее

Real-World Experience Treating SMA With Nusinersen

Nusinersen Treatment for SMAПодробнее

Nusinersen Treatment for SMA

Mechanism of Disease: SMAПодробнее

Mechanism of Disease: SMA

U.S. FDA Approves Biogen’s SPINRAZA™ (nusinersen), The First Treatment for Spinal Muscular AtrophyПодробнее

U.S. FDA Approves Biogen’s SPINRAZA™ (nusinersen), The First Treatment for Spinal Muscular Atrophy

The History of Spinal Muscular Atrophy TreatmentПодробнее

The History of Spinal Muscular Atrophy Treatment

Understanding Spinal Muscular Atrophy (SMA)Подробнее

Understanding Spinal Muscular Atrophy (SMA)

SMA Type 1: How Gene Therapy WorksПодробнее

SMA Type 1: How Gene Therapy Works

Новости