Cut and Paste: Treating Spinal Muscular Atrophy with Nusinersen

Cut and Paste: Treating Spinal Muscular Atrophy with Nusinersen

How Spinraza (nusinersen) and Evrysdi treat Spinal Muscular Atrophy (SMA) through splice-switchingПодробнее

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New Clinical Data on Adult Nusinersen treated Patients with SMAПодробнее

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Treating spinal muscular atrophy in adult patientsПодробнее

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